The US researchers treat the B hemophilia with the gene therapy to obtain the first fruits. American Philadelphia Pediatric hospital’s Katherine · High Dr. and Dr. Standford University medical school Mark · triumphant “Natural Gene Study” on reported in March number that they have carried on the gene therapy security experiment to 3 B hemophiliac, two person of condition obvious changes for the better. Doctor harmless virus which raises specially to the patient intramuscular injection one kind, this kind of virus carries can synthesize the hemoglutination factor IX normal gene. Finally, two patients need to inject the hemoglutination factor IX quantity obvious reduction, the reason are artificially the healthy gene have the function in patient in vivo, makes the hemoglutination factor IX.
Because in vivo lacks the hemoglutination factor, the hemophiliac easy internal hemorrhage and bleeds continues, if to their regular injection hemoglutination factor, the patient does not have life-threatening. B hemophiliac in vivo synthesis hemoglutination factor IX gene existence flaw.